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A Teenager’s Breakthrough Gene Therapy for Sickle Cell Disease
Meet Helen Obando, a shy 16-year-old who likes to dance when her body isn’t ravaged by the debilitating symptoms of sickle cell disease. The genetic blood disorder can cause strokes, organ damage and intense pain that can feel like glass running through her veins.
After a lifetime of pain and potential permanent damage to her body, Helen had the opportunity to receive a breakthrough experimental treatment at Boston Children’s Hospital that would make her the youngest person in the U.S. to have her DNA reset in an attempt to cure her sickle cell disease.
The outcome of her gene therapy could help determine how an estimated 100,000 people in the U.S. and millions more around the world are treated.
+myBinderRelated Content
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education & researchThe Teen Symposium: Engaging Adolescents and Young Adults With Sickle Cell Disease in Clinical Care and ResearchObjective: In the United States, sickle...
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videos & visualsSCDAA Gene Therapy Town Hall – Webinarhttps://www.youtube.com/watch?v=J77Gq9yI...
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education & researchEndocrine and Metabolic Complications in Children and Adolescents With Sickle Cell Disease: An Italian Cohort StudyBackground: Children with Sickle Cell D...
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videos & visualsResearchers Develop Effective Treatment for Sickle Cell Anemiahttps://www.youtube.com/watch?v=7zceTJzH...
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videos & visualsSickle cell adult and pediatric provider interview – Dr Nirmish Shahhttps://www.youtube.com/watch?v=6fFmmPrd...
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news & eventsNHLBI Stepping Up Efforts to Apprise SCD Patients of Therapies and TrialsWide interest in a CBS 60 Minutes story ...
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videos & visualsGene Therapy & Clinical Trials Webinarhttps://www.youtube.com/watch?v=yYexIUgH...
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